Contents

Current Pharmaceutical Biotechnology, Volume 12 - Number 6

Editorial [Hot Topic: Recent Advances in Treatment Approaches of Lysosomal Storage Diseases (LSDs) (Guest Editor: Paula Rozenfeld)]

, 12(6): 853

Paula Rozenfeld


DOI: 10.2174/138920111795542660




Recent Advances in Treatment Approaches to Gaucher Disease

, 12(6): 854 - 860

Deborah Elstein and Ari Zimran


DOI: 10.2174/138920111795542624




Mucopolysaccharidosis Type II (Hunter Syndrome): Clinical Picture and Treatment

, 12(6): 861 - 866

Michael Beck


DOI: 10.2174/138920111795542714




Therapeutic Approaches to the Challenge of Neuronal Ceroid Lipofuscinoses

, 12(6): 867 - 883

R. Kohan, I. A. Cismondi, A. M. Oller-Ramirez, N. Guelbert, V. Tapia Anzolini, G. Alonso, S. E. Mole, R. Dodelson de Kremer and I. Noher de Halac


DOI: 10.2174/138920111795542633




Cell-and Gene-based Therapeutic Approaches for Neurological Deficits in Mucopolysaccharidoses

, 12(6): 884 - 896

Dao Pan


DOI: 10.2174/138920111795542679




New Agents and Approaches to Treatment in Niemann-Pick Type C Disease

, 12(6): 897 - 901

Maria S. Perez-Poyato and Merce Pineda


DOI: 10.2174/138920111795542697




Pompe Disease: From New Views on Pathophysiology to Innovative Therapeutic Strategies

, 12(6): 902 - 915

Giancarlo Parenti and Generoso Andria


DOI: 10.2174/138920111795542606




Treatment of Fabry Disease: Current and Emerging Strategies

, 12(6): 916 - 922

Paula Rozenfeld and Pablo M. Neumann


DOI: 10.2174/138920111795542705




Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Emerging Treatment Strategies

, 12(6): 923 - 930

J. de Ruijter, M. J. Valstar and F. A. Wijburg


DOI: 10.2174/138920111795542651




Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review

, 12(6): 931 - 945

S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki and T. Orii


DOI: 10.2174/138920111795542615




Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients

, 12(6): 946 - 955

Patricia I. Dickson and Agnes H. Chen


DOI: 10.2174/138920111795542642




Recent Advances in Treatment Approaches of Mucopolysaccharidosis VI

, 12(6): 956 - 972

Roberto Giugliani, Clarissa Gutierrez Carvalho, Silvani Herber and Louise Lapagesse de Camargo Pinto


DOI: 10.2174/138920111795542688




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